Fingolimod treatment leads to beneficial effects in Huntington disease (HD), according to a new study in a mouse model of the ...

There were fewer multiorgan transplants in patients with hereditary ATTR-CM with increased use of disease-modifying therapies, a study found.

ATTR-PN diagnosis requires a combination of neurological and non-neurological tests, such as blood pressure monitoring, a ...

Hematopoietic stem cell transplantation seems to be feasible and curative for some patients with MF and splanchnic vein thrombosis, a study found.

The addition of danicopan treatment to background therapy led to improved hemoglobin levels and reduced intravascular and extravascular hemolysis. Researchers have reported long-term results of the ...

rhG-CSF has a short half-life and requires daily injection to maintain an effective blood concentration. Pegylated recombinant human granulocyte colony-stimulating factor (PEG-rhG-CSF) reduced the ...

At Day 100 all but 1 patient were alive and disease-free and at a median follow-up of 47.5 months, 7 patients were alive and disease-free. Hematopoietic stem cell transplantation seems to be feasible ...

Because IgG4-RD affects predominantly older people, these advancements are particularly significant, offering new hope for improving management and outcomes in this age group. New targeted treatments ...

The therapeutic regimen included 2 induction doses of daratumumab within a week, followed by further doses as needed. A combination therapy of daratumumab and romiplostim was successfully used to ...

This case study documents the first known case of concurrent HDFN and FNAIT. A 37-year-old multiparous woman with RhD alloimmunization delivered a preterm neonate at 35 weeks of gestation following ...

The most common variant in the US, Val142Ile, has a reported prevalence of 3%–4% in the African American population. The Val142Ile variant was found in 82.61% of the population who had a pathogenic or ...

Unlike MRI, ultrasound missed a significant proportion of cerebellar hemorrhages, particularly smaller or more subtle lesions. Researchers have proposed a new classification of cerebellar hemorrhage ...