Congenital erythropoietic porphyria (CEP), also known as Günther's disease, is a rare genetic disorder that affects the body's ability to produce heme, a crucial component of hemoglobin in red ...

7.“A few months after getting H1N1 flu, I started sleeping for very long periods of time (up to 20 hours, sometimes two days ...

According to the American Porphyria Foundation (APF), EPP and XLP combined are the third most common porphyria, with an incidence of possibly two to five per million people, and are the most ...

7.“A few months after getting H1N1 flu, I started sleeping for very long periods of time (up to 20 hours, sometimes two days ...

GIVLAARI for the treatment of adults with acute hepatic porphyria; and OXLUMO for the treatment of primary hyperoxaluria type 1. In addition, the company develops patisiran for the treatment of ...

A woman revealed that consuming garlic, which contains sulphur, can be life-threatening for her because she suffers from 'vampire disease.' WHAT IS VAMPIRE DISEASE? Acute intermittent porphyria ...

In this review of RNA therapies, we paint an overview of what’s going on in a field that is addressing a number of diseases.

But life for the king was far from idyllic. George's first attack of madness --actually the rare blood disorder porphyria, which caused severe abdominal pain, extreme perspiration, dark red urine ...

Disc Medicine finalised the pivotal Phase III trial design of bitopertin in erythropoietic protoporphyria (EPP) with the FDA ...

Givlaari is approved for the treatment of acute hepatic porphyria. Oxlumo is approved for treating primary hyperoxaluria type 1 (PH1) to lower urinary oxalate levels in pediatric and adult patients.

Equities research analysts at Zacks Research upped their Q1 2026 earnings per share (EPS) estimates for Alnylam Pharmaceuticals in a research report issued to clients and investors on Monday, January ...