Zevra to receive a 2025 New Treatment Award for MIPLYFFA™ at the 21st Annual WORLDSymposiumEight abstracts discussing data and clinical ...

According to the open letter, the delay in rolling out the proposed ₹ 974 crore national programme on rare diseases has exacerbated these challenges, leaving patients, most of whom are children, in ...

Patient advocacy groups warned that delays in implementing India's rare disease policy have left many, including children, in ...

JCR Pharmaceuticals Co., Ltd. (TSE 4552; "JCR") announced today that it will present at the 21st Annual WORLDSymposiumtm 2025, held February 3-7, 2025, in San Diego, Calif. The poster presentations ...

Patient advocacy groups have written to Union Health Minister J.P. Nadda, raising concerns about the delay in rolling out the ...

Denali Therapeutics DNLI has performed well in the past 12 months amid a volatile market. Shares of the company have gained ...

When I look for the best cloud storage for photos, I always look for services that offer plenty of storage space for high-definition photos with secure online backups at a reasonable price.

These molecules, upregulated in cancer cells, are excreted through a surprising mechanism—lysosomal exocytosis. Researchers published their results in the Journal of Cell Biology on January 3 ...

Inflammatory bowel disease (IBD) is a group of intestinal disorders that cause prolonged inflammation of the digestive tract. It can include ulcerative colitis (UC) or Crohn’s disease.

I'm a cloud and data expert - here's my verdict on the best cloud storage services around right now The best cloud storage services should provide a secure space in the cloud for you to store all ...

Batten disease refers to a group of inherited ... enteric neuron degeneration and extends survival in lysosomal storage disorder mouse models, Science Translational Medicine (2025).