Fingolimod treatment leads to beneficial effects in Huntington disease (HD), according to a new study in a mouse model of the ...

There were fewer multiorgan transplants in patients with hereditary ATTR-CM with increased use of disease-modifying therapies, a study found.

ATTR-PN diagnosis requires a combination of neurological and non-neurological tests, such as blood pressure monitoring, a ...

Because IgG4-RD affects predominantly older people, these advancements are particularly significant, offering new hope for improving management and outcomes in this age group. New targeted treatments ...

rhG-CSF has a short half-life and requires daily injection to maintain an effective blood concentration. Pegylated recombinant human granulocyte colony-stimulating factor (PEG-rhG-CSF) reduced the ...

At Day 100 all but 1 patient were alive and disease-free and at a median follow-up of 47.5 months, 7 patients were alive and disease-free. Hematopoietic stem cell transplantation seems to be feasible ...

It is important to include IgG4-RD in the differential diagnosis when investigating other immune-related conditions. An elderly man with constrictive pericarditis was diagnosed with immunoglobulin ...

An initial diagnosis of neurosarcoidosis was questioned when the patient did not respond to therapy with prednisolone and infliximab. A patient with a 10-year history of relapsing chronic lymphocytic ...

As the year comes to a close and a new year begins, I look back on all the challenging moments and triumphs of a year living with myasthenia gravis (MG). It’s easy to fixate on the difficulties ...

This last year living with Pompe disease has been overall good. But it has also been a rollercoaster of emotions. Some were good and some were sad. The best thing that happened to me in 2024 was ...

(Getty Images) Rare antigens, ill-defined guidelines, and shortcomings in screening are among the challenges clinicians face in diagnosing and treating FNAIT. Fetal and neonatal alloimmune ...

I have had cold agglutinin disease (CAD), a rare form of autoimmune hemolytic anemia (AIHA) for about 4 years. I have gotten used to the signs and symptoms I experience when I get cold, whether that ...