BENGALURU: Bengaluru-based Narayana Nethralaya is developing gene therapy solutions that could drastically reduce the cost of ...

Parents of children with Spinal Muscular Atrophy (SMA), a rare disease, say the budget is mere eyewash; custom duty exemption ...

Finance Minister Nirmala Sitharaman announced a full exemption from basic customs duty (BCD) for 36 live-saving drugs to ...

A Wentzville mother Allyson Jercick said this van has changed her 8-year-old son's life. ST CHARLES, Mo. — We often hear about the season of giving exclusively at the end of each year, but some people ...

The impact of Mayhill’s continued support extends beyond the van. Over the past 15 years, he and his team have given away 12 ...

South San Francisco, CA, January 30, 2025 – The California Institute for Regenerative Medicine (CIRM), one of the world’s largest institutions dedicated to regenerative medicine, has awarded nearly ...

Barbara Goodfriend, 83, opted for medical aid in dying after being diagnosed with ALS. The New Jersey widow ended her life in ...

A retrospective analysis showed IV edaravone in participants with ALS was associated with fewer reported disease progression milestones and deaths than control.

A live audio webcast of the fireside chat presentation will be available at https://wsw.com/webcast/guggen2/kros/2033361 and an archived replay will be accessible in the Investors section of the Keros ...

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

The gene therapy delandistrogene moxeparvovec-rokl showed clinically meaningful benefits and disease stabilization at 2 years ...