Muscular dystrophy (MD) represents a group of inherited muscle disorders that primarily cause muscle weakness and muscle wasting, though some types of the disease also present with other ...

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National Ambassador. Sander joins MDA National Ambassador Ira Walker from Fort ...

Muscular dystrophy can appear in infancy up to middle age or later, and its form and severity are determined in part by the age at which it occurs. Some types of muscular dystrophy typically ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Celebrating 75 Years of Progress, Legacy, Impact, and Momentum Leading up to Rare Disease Day on February 28 Muscular ...

A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...

Myopathic (myo = muscle, pathy = disease) conditions can include polymyositis ... The rate of progression of the muscular dystrophies depends on the type of dystrophy. While some progress slowly, ...

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a treatment for adults over 25, but he argues that time is running out in his case.

Only males can get certain types of muscular dystrophy because of how the disease is inherited. Children who are born with muscular dystrophy usually develop normally for the first few years of life.

Altruism values for treatments of rare, severe pediatric diseases have not been estimated. This study found the altruism value for a hypothetical new Duchenne muscular dystrophy treatment to be $ ...

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early diagnosis, multidisciplinary care, and emerging treatments like gene therapy ...

Johnny Quintana’s life changed at the age of 19 when he was diagnosed with a rare form of muscular dystrophy called ...