GEN1 天
Optimizing AAV Gene Delivery: Hitting the Target Safely and Effectively
Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.
ophthalmologytimes2 天
Gene therapy voretigene neparvovec boosts vision in pediatric IRD patients
Previous research has shown that voretigene neparvovec administered subretinally early in childhood for RPE65-mediated ...