Charcot-Marie-Tooth (CMT) disease, a group of heritable disorders that affect the peripheral nerves, is marked by specific genetic changes. Research by the team of Prof. Ludo Van Den Bosch (VIB-KU ...

The US Food and Drug Administration (FDA) has granted orphan drug designation (ODD) to NMD Pharma’s oral lead development programme, NMD670, designed to treat Charcot-Marie-Tooth disease (CMT).

NMD670 is an oral therapy designed to treat Charcot-Marie-Tooth disease. Credit: SkazovD / Shutterstock. The US Food and Drug Administration (FDA) has granted orphan drug designation (ODD) to NMD ...

Objective To identify the genetic characteristics in a large-scale of patients with Charcot-Marie-Tooth disease (CMT). Methods From May 2012 to August 2016, we collected 1005 cases with suspected CMT ...

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National Ambassador. Sander joins MDA National Ambassador Ira Walker from Fort ...

French biotech Pharnext has seen the value of its shares collapse after it revealed that its lead drug, a treatment for Charcot-Marie-Tooth (CMT) disease, failed to make the grade in a phase 3 trial.

This novel treatment approach has resulted in clinical evidence of CIC-1 inhibition in myasthenia gravis and preclinical evidence in spinal muscular atrophy, Charcot-Marie tooth disease and sarcopenia ...

This novel treatment approach has resulted in clinical evidence of CIC-1 inhibition in myasthenia gravis and preclinical evidence in spinal muscular atrophy, Charcot-Marie Tooth disease and sarcopenia ...

The country icon revealed in 2021 that he had been living with a degenerative nerve condition called Charcot-Marie-Tooth disease, which causes nerve damage, primarily in the arms and legs.

More commonly, however, it is the result of Charcot-Marie Tooth disease, a hereditary disorder in which the conduction speed of nerves slow over time and causes weakness of the distal muscles of the ...